INDUSTRY SYMPOSIUM // SAREPTA - A Deep Dive Into LGMDs: Disease, Diagnosis, and the Developing Treatment Landscape

• SYMP1L1 • Overview of Limb-Girdle Muscular Dystrophies: Exploring the underlying pathology > E. Erik NIKS (Leiden, The Netherlands) • SYMP1L2 • The Evolving Diagnostic Process: Accurate diagnosis is needed to identify management opportunities > G. Giacomo COMI (Milan, Italy) • SYMP1L3 • Exploring New Therapies: Investigational SRP-9003 for LGMD2E/R4 > L. Linda LOWES (Columbus, Ohio State, Usa) • SYMP1L4 • Q&A session