YOUNG INVESTIGATORS SYMPOSIUM

14:00 • S5L1 • Muscle targeted gene therapy to cure BIN1 centronuclear myopathy > J. Jacqueline JI (Illkirch-Graffenstaden, France) 14:15 • S5L2 • RNA-sequencing of Type II SMA paravertebral muscle after treatment reveals distinct molecular subtypes. > F. Fiorella GRANDI (Paris, France) 14:30 • S5L3 • The damaged lysosome is a therapeutic target for combined therapy in Duchenne muscular dystrophy > A. Abbass JABER (Evry, France) 14:45 • S5L4 • Deciphering the consequences of SORBS1 mis-splicing in myotonic dystrophy type 1 > M. Morgan GAZZOLA (Corbeil-Essonnes, France)